PTC Therapeutics, Inc

Bronze Sponsor

Focus: Duchenne muscular dystrophy, gene therapy & CNS disorders, hATTR Amyloidosis, familial chylomicronemia syndrome, SMA, and oncology

https://www.ptcbio.com/

PTC is a science-led, global biopharmaceutical company focused on the discovery, development and commercialization of clinically-differentiated medicines to patients with rare disorders. PTC's ability to globally commercialize products drives investment in a pipeline, and our mission to provide access to treatments for patients who have an unmet medical need.